Muscular dystrophy is a disease caused by mutations in the dystrophin gene. The muscles of muscular dystrophy patients weaken and atrophy over time. Heart and breathing muscles may also eventually be ...
Atamyo Therapeutics, a biotechnology company specializing in the development of next-generation gene therapies for limb-girdle muscular dystrophy (LGMD), announced at the MDA (Muscular Dystrophy ...
12-year-old Deklan Locke, who has Duchenne muscular dystrophy, uses a power wheelchair and raises awareness about the disease. Duchenne muscular dystrophy is a rare genetic disorder that causes muscle ...
An El Paso mother traveled to Washington, D.C., this week to advocate for her 14-year-old son, who is living with a rare ...
StitchR, a new gene therapy technique, delivers large genes in two parts to treat muscular dystrophies by restoring critical proteins in animal models. Gene therapy can effectively treat various ...
Riley Moser is a digital producer who covers breaking news and feature stories for CBS Minnesota. Riley started her career at CBS Minnesota in June 2022 and earned an honorable mention for sports ...
Europe’s Committee for Medicinal Products for Human Use (CHMP) has recommended granting a conditional marketing authorization for Duvyzat (givinostat, Italfarmaco) to treat Duchenne muscular dystrophy ...